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April 16, 2025

FDA Grants RMAT Designation to Atsena Therapeutics’ Gene Therapy for X-linked Retinoschisis

The designation aims to expedite development of ATSN-201 for X-linked retinoschisis, a rare inherited retinal disease with no approved treatment.The…

Atsena Therapeutics IRD FDA Fast Track 01
March 13, 2025

Atsena Secures FDA Fast Track Designation for ATSN-201 to Treat X-Linked Retinoschisis

With no approved treatments for XLRS, another promising gene therapy enters the fray. Atsena Therapeutics (North Carolina, USA) announced that…

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