FDA Grants Rare Pediatric Disease Designation to Ocugen’s Gene Therapy for Stargardt Disease
Ocugen’s OCU410ST gene therapy lands a rare badge of honor in the fight against IRDs. The U.S. Food and Drug…
FDA Grants Breakthrough Therapy Designation to Belite Bio’s Tinlarebant for Stargardt Disease
A once-daily oral pill for Stargardt? Tinlarebant takes a big step with FDA breakthrough status. In a major step forward…